Wednesday, June 24, 2020
Research Theme(s): Translational Genomics

LOS ANGELES — Investigators at The Lundquist Institute have teamed up with the Cure Sanfilippo Foundation for a unique clinical trial that explores whether repurposing an existing anti-inflammatory drug can provide relief to children suffering from Sanfilippo syndrome. Often referred to as “childhood Alzheimer’s,” Sanfilippo is a metabolic disorder that leads to rapid neurological deterioration, suffering, and ultimately death.

Wednesday, June 24, 2020
Research Theme(s): Translational Genomics

LOS ANGELES — Investigators at The Lundquist Institute have teamed up with the Cure Sanfilippo Foundation for a unique clinical trial that explores whether repurposing an existing anti-inflammatory drug can provide relief to children suffering from Sanfilippo syndrome. Often referred to as “childhood Alzheimer’s,” Sanfilippo is a metabolic disorder that leads to rapid neurological deterioration, suffering, and ultimately death.